MAKING RAREMARKABLE MOMENTS

A raremarkable unmet need

In Latin, “mirum” means remarkable, wondrous, or extraordinary. Here at Mirum, we see beyond rare diseases—we see the people. With creativity and heart, we light the way for those searching for hope. Because every breakthrough we make is not just medicine—it’s a moment of joy, a chance for patients to live fully. What we do at Mirum is nothing short of “raremarkable.” That’s why our name is so fitting.

See What Guides Us

Developing raremarkable medicines with the potential to change lives

Where others see unmet need solely as a treatment gap, we envision a unique opportunity to revitalize a community like never before. Our need to develop transformative medicine is propelled by our passion for patients and their loved ones and we’re focused on turning possibilities into realities.

Learn about our science

Transformative scientific discoveries

Driven by data and meaningful evidence, we are dedicated to transforming scientific discoveries into therapies poised to change the trajectory of rare diseases for generations to come.

Explore what’s in development

Meet some raremarkable people

Patients and families living with rare diseases are at the center of everything we do. We invite you to meet some of the people in this community and learn more about living with rare disease.

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